Is this you? As a journalist, you can create a free Muck Rack account to customize your profile, list your contact preferences, and upload a portfolio of your best work.
Claim your profile
Duchenne muscular dystrophy (DMD) is a progressive X-linked muscle-wasting disease, caused by mutations in the dystrophin gene. Despite the recent approval of the first gene therapy for DMD, current gene therapy produces a shortened micro-dystrophin with variable and incomplete expression and associated with high risk of serious complications (Mendell et al., 2025).
As a journalist, you can create a free Muck Rack account to customize your profile, list your contact preferences, and upload a portfolio of your best work.
