1School of Medicine, Tel Aviv University, Tel Aviv, Israel 2Gaucher Unit, The Eisenberg R&D Authority, Shaare Zedek Medical Center, Jerusalem, Israel 3Faculty of Medicine, Hebrew University, Jerusalem, Israel 4Braun School of Public Health and Community Medicine, Hebrew University, Jerusalem, Israel 5MaccabiTech, Maccabi Healthcare Services, Tel Aviv, Israel 6Intensive Care Unit, Rambam Health Care Campus, Haifa, Israel 7Takeda Pharmaceuticals International AG, Zurich, Switzerland 8Takeda...