Joëll Bense

1 INTRODUCTION Patient-reported outcomes (PROs) are increasingly applied in hematopoietic stem cell transplantation (HSCT) for the purpose of collecting data for research or monitoring symptoms.1, 2 However, PROs can also be used to better understand the patients' needs, and to support shared decision-making (SDM).3, 4 Integrating PROs into routine care offers the healthcare provider (HCP) the opportunity to identify essential topics and address problems early on, provide personalized...

BMF bone marrow failure CC chronic condition COVID-19 coronavirus disease 2019 DT-P Distress Thermometer for Parents GvHD graft-versus-host disease HB hemoglobinopathies HSCT hematopoietic stem cell transplantation IEI inborn errors of immunity 1 INTRODUCTION Allogeneic hematopoietic stem cell transplantation (HSCT) is an established curative treatment for an increasing number of patients with large variety of inherited or acquired nonmalignant diseases.1 Survival rates have continued to...

1 Introduction Primary immunodeficiency disease (PID) refers to inherited diseases caused by genetic variants of immunoregulatory proteins, resulting in impairment of the immune system (1, 2). PID is primarily characterized by increased susceptibility to infections but can also result in autoimmune diseases, autoinflammatory diseases, and malignancies (1, 2).