Conflicts of Interest Christine L. Kempton has received honoraria from Spark Therapeutics, Octapharma, Genetech and Pfizer and research support from Novo Nordisk. Tyler W. Buckner has acted as a paid consultant to BioMarin, Tremeau Pharmaceuticals and UniQure and has participated in advisory boards with Takeda, Tremeau, Novo Nordisk, Genentech/Roche, Spark, Pfizer, Bayer and Kedrion. All other authors have no disclosures.